WebSpinal muscular atrophy (SMA) is a severe and often devastating neurologic disorder of infants and chil-dren. The clinical spectrum extends from the most ... Clinical trials for … WebPhase 3, Double-Blind, Placebo-Controlled Trial to Evaluate the Efficacy and Safety of Apitegromab (SRK-015) in Patients With Later-Onset Spinal Muscular Atrophy Receiving …
Spinal muscular atrophy: a clinical and research update
WebJul 27, 2024 · Clinical Trial Finder Jewelfish A Study of RO7034067 in Adult and Pediatric Participants With Spinal Muscular Atrophy (JEWELFISH) Spinal Muscular Atrophy (SMA) Trial Status: Active, not recruiting This trial runs in 9 Countries Trial Identifier: NCT03032172 2016-004184-39 BP39054 Show Clinical Trial Results Clinical Trial Results WebFind out more about the clinical trial for [Spinal Muscular Atrophy (SMA)]. This study will evaluate the pharmacokinetics (PK) and safety of risdiplam in participants ... Use our trial search to find descriptions of clinical trials, participating trial clinics, their recruitment status and results. Find clinical trials russian wedding cakes recipe
Spinal muscular atrophy — Johns Hopkins University
WebApr 11, 2024 · Currently, the only approved gene therapy for the treatment of spinal muscular atrophy (SMA) is onasemnogene abeparvovec (Zolgensma; Novartis), indicated … WebAbout The SMA Clinic At the Pediatric SMA Clinical Research Center, a neurologist with expertise in SMA and pediatric neuromuscular disease conducts the SMA evaluation. The first step in being evaluated is to be examined by our team of physicians at the clinic. A thorough neurological examination will be conducted and previous tests reviewed. WebJul 27, 2024 · Spinal Muscular Atrophy (SMA) Trial Status: Active, not recruiting This trial runs in 10 Countries Trial Identifier: NCT03779334 BN40703 + − Show trial locations For Expert The source of the below information is public registry websites such as ClinicalTrials.gov, EuClinicalTrials.eu, ISRCTN.com, etc.. schedule insanity max 30